#gene-therapy

5 briefings

FDA Halts Regenxbio Gene Therapy Trial After Spinal Masses Found in Five Patients

Aug 25, 2026, 10:28 PM

FDA Clears Ultragenyx's Genglycos, the Company's First Gene Therapy

Aug 22, 2026, 9:06 PM

Vertex's Casgevy Gene Therapy Cleared to Treat Kids With Sickle Cell

Jul 3, 2026, 8:12 AM

Regenxbio Will Resubmit Hunter Syndrome Gene Therapy to FDA — No New Study Required

Jun 22, 2026, 3:22 PM

uniQure Soars 66% as FDA Clears Path for Huntington's Gene Therapy

Jun 17, 2026, 8:14 PM